Private, focused on the development of IV Citrulline for rare pediatric diseases. First indication, the prevention of significant sequelae of pediatric acute cardiopulmonary bypass-induced lung injury, Ph 3 trial is ongoing. After receiving FDA and EMA registration, the company sold Cholbam, for bile acid synthesis defects and peroxisomal disorders, to Retrophin (RTRX) in 2015, providing an ongoing, quarterly revenue stream.
Autoimmune, Metabolic Disorders, Rare Disease
729 E. Pratt St
Baltimore, MD 21202
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